FDA Approvals

BioMarin pads case for Voxzogo expansion as achondroplasia competition field shifts

FiercePharma 1h ago Phase 3

With a phase 3 win now fleshed out and an FDA filing recently submitted, BioMarin is advancing expansion plans for Voxzogo, looking to extend the dwarfism drug’s reach as it faces new pressure in its inaugural achondroplasia indication.

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